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X-linked Adrenoleukodystrophy Trial in Beijing

Recruiting
  • X-linked Adrenoleukodystrophy
    • Beijing, China
      Beijing Tiantan Hospital
    Jul 2, 2023

    X-linked Hypophosphatemia Trial in Vienna (Foot X rays, Clinical examination + scores)

    Completed
    • X-linked Hypophosphatemia
    • Foot X rays
    • Clinical examination + scores
    • Vienna, Austria
      Orthopedic Hospital Speising Vienna
    Oct 5, 2023

    Using Brain Diffusion MRI in X-linked Adrenoleukodystrophy

    Not yet recruiting
    • X-linked Adrenoleukodystrophy
    • brainQuant module of brainTale-care platform
    • (no location specified)
    Jun 12, 2023

    X-linked Retinoschisis Trial (ATSN-201)

    Not yet recruiting
    • X-linked Retinoschisis
    • ATSN-201
    • (no location specified)
    May 26, 2023

    X-linked Retinoschisis Trial in Xiaogan (ZM-01-L, ZM-01-H)

    Recruiting
    • X-linked Retinoschisis
    • Xiaogan, Hubei, China
      Wuhan University Renmin Hospital affiliated with Hanchuan Hospit
    Sep 29, 2023

    X-linked Retinoschisis Trial in Shanghai (LX103 Injection)

    Recruiting
    • X-linked Retinoschisis
    • LX103 Injection
    • Shanghai, China
      Shanghai General Hospital, Shanghai Jiao Tong University
    Apr 4, 2023

    X-Linked Dystonia Parkinsonism Trial in Manila (transcranial magnetic resonance-guided focused ultrasound pallidothalamic

    Available
    • X-Linked Dystonia Parkinsonism
    • transcranial magnetic resonance-guided focused ultrasound pallidothalamic tractotomy
    • Manila, Philippines
      Philippine General Hospital
    Aug 21, 2022

    X-Linked Retinitis Pigmentosa Trial in Beijing, Shanghai (FT-002)

    Recruiting
    • X-Linked Retinitis Pigmentosa
    • FT-002
    • Beijing, Beijing, China
    • +1 more
    May 23, 2023

    Japanese Participants With X-linked Retinitis Pigmentosa

    Recruiting
    • X-Linked Retinitis Pigmentosa
      • Tokyo, Japan
        National Hospital Organization Tokyo Medical Center
      Jan 3, 2023

      X-Linked Retinitis Pigmentosa Trial in Meguro-ku (AAV5-hRKp.RPGR)

      Not yet recruiting
      • X-Linked Retinitis Pigmentosa
      • AAV5-hRKp.RPGR
      • Meguro-ku, Japan
        National Hospital Organization Tokyo Medical Center
      Jun 23, 2023

      Clinical and Genetic Studies of X-Linked Juvenile Retinoschisis

      Recruiting
      • Retinoschisis
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Jan 25, 2023

        Patients With X-linked Retinitis Pigmentosa (XLRP)

        Completed
        • X-Linked Retinitis Pigmentosa
          • Durham, North Carolina
          • +2 more
          Jan 10, 2023

          Severe Combined Immunodeficiency Disease, X-linked Trial in San Francisco, Memphis, Seattle (genetic, drug, device)

          Recruiting
          • Severe Combined Immunodeficiency Disease, X-linked
          • CL20-i4-EF1α-hγc-OPT
          • +2 more
          • San Francisco, California
          • +2 more
          Jan 9, 2023

          X-linked Adrenoleukodystrophy Trial in Leipzig (SMART-ALD, Waiting list)

          Recruiting
          • X-linked Adrenoleukodystrophy
          • SMART-ALD
          • Waiting list
          • Leipzig, Saxony, Germany
          • +1 more
          Aug 16, 2022

          X-linked Severe Combined Immunodeficiency (XSCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)

          Suspended
          • X-linked Severe Combined Immunodeficiency (XSCID)
          • Bethesda, Maryland
            National Institutes of Health Clinical Center, 9000 Rockville Pi
          Aug 24, 2022

          Quality of Life in Women With X-linked Adrenoleukodystrophy

          Recruiting
          • X-linked Adrenoleukodystrophy
            • Leipzig, Saxony, Germany
              Leipzig University Medical Center, Leukodystrophy Outpatient Cli
            Apr 4, 2022

            X-linked Hypophosphatemia, Hypophosphatemic Rickets, Hypophosphatemic Rickets, X-Linked Dominant Trial in Boston (Calcitriol)

            Recruiting
            • X-linked Hypophosphatemia
            • +2 more
            • Boston, Massachusetts
              Massachusetts General Hospital
            Mar 16, 2022

            X-linked Adrenoleukodystrophy Trial in Palo Alto (vitamin D3)

            Completed
            • X-linked Adrenoleukodystrophy
            • vitamin D3
            • Palo Alto, California
              Stanford University
            Jun 6, 2022

            X-Linked Retinitis Pigmentosa

            Completed
            • X-Linked Retinitis Pigmentosa
            • Other: Assessments
            • Phoenix, Arizona
            • +21 more
            Jan 17, 2023

            Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and

            Recruiting
            • Granuloma
            • +4 more
              • Bethesda, Maryland
                National Institutes of Health Clinical Center
              Jan 25, 2023

              Burden of Disease and Functional Impairment in XLH

              Recruiting
              • X Linked Hypophosphatemia
              • no intervention
              • Wuerzburg, Germany
                Orthopedic Center for Musculoskeletal Research, Orthopedic Depar
              Aug 30, 2022

              Fragile X Syndrome, Fragile X Mental Retardation Syndrome, Mental Retardation, X Linked Trial in Sacramento (Placebo Medication,

              Active, not recruiting
              • Fragile X Syndrome
              • +9 more
              • Sacramento, California
                UC Davis MIND Institute
              Feb 22, 2022

              X-linked Hypophosphatemic Rickets/Osteomalacia in Collaboration

              Recruiting
              • X-Linked Hypophosphatemia
              • no intervention
              • Osaka, Japan
                Osaka University Hospital
              Feb 9, 2022

              Severe Combined Immunodeficiency, X-Linked Trial in London (Lentiviral vector transduced CD34+ cells)

              Recruiting
              • Severe Combined Immunodeficiency, X-Linked
              • Lentiviral vector transduced CD34+ cells
              • London, Greater London, United Kingdom
                Great Ormond Street Hospital for Children NHS Foundation Trust
              Mar 15, 2022

              X-Linked Myotubular Myopathy (XLMTM) Subjects

              Completed
              • X-linked Myotubular Myopathy
                • Los Angeles, California
                • +7 more
                Jul 27, 2022